Booster toward new scientific breaktroughs in rare and pediatric diseases

ABOUT THE MOONSHOT

95% of the 6,000-7,000 identified rare diseases don’t have an approved therapy. For most of these diseases, research is effectively non-existent. The search for new treatments is thwarted by enormous scientific challenges. At the current pace, it would take over 100 years to develop treatments for all rare conditions.

Public-private partnerships could help pool resources to solve problems more quickly, reduce fragmentation and scale up existing initiatives to make a real difference for patients. That’s why a coalition of partners is joining forces to accelerate research in rare and paediatric diseases and bring new therapies to patients.

Latest news

18 Oct 2024

Virtual Event – Innovating for Impact: Shaping the Future of Rare Disease Treatment

Millions of Europeans are living with rare diseases where no treatment option exists. How can the work from the public and private sector help in accelerating research and raise awaren...
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16 Apr 2024

Translational research needs recommendations

The Rare Diseases (RD) Moonshot was set up to boost public private collaborations in the areas where there are with no treatment options and there is no R&D going on.    The RD Moonshot part...
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29 Feb 2024

Rare Disease Moonshot supports the EURORDIS-Rare Diseases Europe’s call for an EU action plan for Rare Diseases

On the rarest of days, we, the members of the Rare Diseases Moonshot, stand together to celebrate the resilience, strength, and perseverance of those living with rare diseases. This day serves as...
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